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Neuren’s Phase 3 NNZ-2591 Trial for Phelan-McDermid Syndrome is Now Active!

Neuren’s Phase 3 NNZ-2591 Trial for Phelan-McDermid Syndrome is Now Active!

The Phelan-McDermid Syndrome Foundation is sharing an important update with our community: Neuren’s Phase 3 clinical trial of NNZ-2951, known as the “Koala” study, is now active and listed on clinicaltrials.gov.  

Continue ReadingNeuren’s Phase 3 NNZ-2591 Trial for Phelan-McDermid Syndrome is Now Active!
Jaguar Gene Therapy Community Letter & FAQ *UPDATED 2/23/26*

Jaguar Gene Therapy Community Letter & FAQ *UPDATED 2/23/26*

A new FAQ from Jaguar Gene Therapy is now available, including updated details about the JAG201 clinical study. This FAQ addresses…

Continue ReadingJaguar Gene Therapy Community Letter & FAQ *UPDATED 2/23/26*
Neuren Phase 2 trial Investor Presentation

Neuren Phase 2 trial Investor Presentation

Neuren has released a statement that the drug was found to be generally safe at the dose tested, having no serious adverse effects.

Continue ReadingNeuren Phase 2 trial Investor Presentation
Press Release – Neuren Phase 2 trial shows significant improvements in Phelan-McDermid syndrome

Press Release – Neuren Phase 2 trial shows significant improvements in Phelan-McDermid syndrome

Neuren has released a statement that the drug was found to be generally safe at the dose tested, having no serious adverse effects.

Continue ReadingPress Release – Neuren Phase 2 trial shows significant improvements in Phelan-McDermid syndrome

Clinical Research Decision Tool

Use this chart to help you make an informed decision when considering participation in a clinical trial.

Continue ReadingClinical Research Decision Tool

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