Today, 12/14/21, Jaguar Gene Therapy announced that it is targeting SHANK3 for gene therapy.
PMSF has been meeting monthly with the Jaguar team, and can report that their patient advocacy focus and interest in our input this early has been a great asset. Please read the letter from their CEO and review the FAQs. This work is still being tested in pre-clinical animal models and has not yet been tested in humans. It is still early and there is much to learn.
Click here to read the letter from Jaguar Gene Therapy’s CEO.