Piloting Treatment with IGF-1 in Phelan-McDermid Syndrome

By Geraldine Bliss, Board Member and Research Liaison

Since 2012, the Seaver Autism Center at the Icahn School of Medicine at Mt. Sinai has been enrolling individuals with PMS in a clinical trial of IGF-1.

The findings from the first pilot study were published here:  https://www.ncbi.nlm.nih.gov/pubmed/25685306

Read an update from Dr. Alex Kolevzon, the lead investigator, reporting findings from the second pilot study.